Targeted Therapies

Timely Information for Practicing Physicians

www.tgt-therapies.com

AUGUST 2005

MULTIPLE MYELOMA

Bortezomib vs high-dose dexamethasone. Paul Richardson and colleagues conducted a multicenter, open-label, phase III study in which 669 patients with relapsed multiple myeloma were randomized (1:1) to receive the proteasome inhibitor bortezomib or standard therapy with high-dose dexamethasone. Bortezomib 1.3 mg/m2 was administered intravenously on days 1, 4, 8, and 11 every 21 days for 8 cycles and on days 1, 8, 15, and 22 every 35 days for 3 cycles for a maximum treatment period of 273 days. Dexamethasone 40 mg was administered orally on days 1–4, 9–12, and 17–20 every 35 days for 4 cycles and on days 1–4 every 28 days for 5 cycles for a maximum treatment period of 280 days. Patients treated with bortezomib had higher overall and complete response rates (38% vs 18%; P <0.001 and 6% vs <1%; P <0.001, respectively) than patients treated with dexamethasone. The median time to progression was 6.2 months for the bortezomib group and 3.5 months for the dexamethasone group (P <0.001). In addition, the survival rate at 1 year was greater in bortezomib group than in the dexamethasone group (80% vs 66%; P = 0.003). Grade 3 or 4 adverse events were reported in 75% and 60% of patients in the bortezomib and dexamethasone groups, respectively. These results demonstrated that bortezomib is a more effective therapy than high-dose dexamethasone for patients with relapsed multiple myeloma. (Richardson PG, et al. N Engl J Med. 2005;352:2487–2498)

 

CHRONIC LYMPHOCYTIC LEUKEMIA (CLL)

Fludarabine, cyclophosphamide, rituximab (FCR) combination therapy. The results of 2 studies investigating the use of FCR in CLL patients were recently reported. William Wierda and others administered 6 cycles of FCR to 177 patients with previously treated CLL (34 patients [19%] had previously received FC). The overall and complete response (CR) rates were 73% and 25%, respectively. Twelve (32%) of 37 complete responders tested achieved molecular remissions in bone marrow. Myelosuppression was the most common toxicity. Grade 4 neutropenia, grade 4 thrombocytopenia, and grade 3 or 4 anemias occurred in 66%, 18%, and 24% of patients, respectively. In the second study, Michael Keating and colleagues treated 224 patients with previously untreated advanced CLL with 6 cycles of FCR. The overall response rate was 95%, and CR was achieved in 70% of patients. Fewer than 1% CD5- and CD19-coexpressing cells were detected in bone marrow after therapy in 138 (67%) of 207 patients tested. Grade 3 or 4 neutropenia occurred during 52% of the treatment courses and one third of the patients had more than one episode of infection. Thus, FCR produced high CR rates in both previously treated and previously untreated CLL populations. In addition, several patients achieved flow cytometric and molecular remissions. However, FCR therapy was associated with a high rate of severe myelosuppression and infection. Long-term follow-up is needed to confirm the clinical benefit of this therapy. An editorial by Thomas Lin and others cautions that because the Keating trial of treatment-naïve patients is a phase II noncomparative study, it is not appropriate to compare these results with those of previous studies as the effect of demographic features on efficacy outcomes is not known in the absence of a control arm. (Wierda W, et al. J Clin Oncol. 2005;23:4070–4078, Keating MJ, et al. J Clin Oncol. 2005;23:4079–4088, and Lin TS, et al. J Clin Oncol 2005;23:4009–4012.)

 

NON-HODGKIN’S LYMPHOMA (NHL)

Long-term results of rituximab plus CHOP (R-CHOP) in diffuse large B-cell lymphoma (DLBCL). Pierre Feugier and associates analyzed the long-term outcomes of elderly patients with DLBCL treated in a study comparing CHOP (cyclophosphamide, doxorubicin, vincristine, and prednisone) with R-CHOP. With a median follow-up of 5 years, event-free, progression-free, disease-free, and overall survival remained statistically superior in patients treated with R-CHOP than with CHOP. No long-term toxicities were reported in patients treated with R-CHOP. The authors suggest that R-CHOP become the standard regimen for treating elderly patients with DLBCL. (Feugier P, et al. J Clin Oncol 2005;23:4117–4126)

 

Myelodysplasia and acute myeloid leukemia following NHL therapy. Two papers report treatment-related myelodysplastic syndromes (MDS) and acute myeloid leukemia (AML) after fludarabine, mitoxantrone, and dexamethasone (FND)-containing regimens or monoclonal antibody therapies for patients with NHL. After a median follow-up of 5 years, MDS was observed in some patients following therapy with FND while no cases of MDS/AML were reported in 76 patients receiving I131 tositumomab as initial therapy. An analysis of 995 patients with NHL who had been treated with tositumomab and I131 tositumomab with or without previous chemotherapy showed the annualized incidence of MDS/AML to be no greater than that expected after the patients' prior chemotherapy. (Bennett JM, et al. Blood 2005;105:4576–4582 and Mclaughlin P, et al. Blood 2005;105:4573–4575)

 

BREAST CANCER

Addition of trastuzumab to chemotherapy improves neoadjuvant results. Aman Buzdar and colleagues randomized patients with HER2-positive operable breast cancer to 4 cycles of paclitaxel followed by 4 cycles of epirubicin, cyclophosphamide, and fluorouracil or the same regimen with weekly trastuzumab for 24 weeks. After the completion of neoadjuvant therapy, patients underwent segmental or total mastectomy and an evaluation for axillary disease. The trial's data monitoring committee stopped the study after 34 patients had completed therapy due to the superior results observed in the trastuzumab plus chemotherapy group. The pathologic complete response (pCR) rates were 25% and 66.7% in the chemotherapy alone and trastuzumab plus chemotherapy groups, respectively (P = 0.02). A decrease of >10% in cardiac ejection fraction developed in 5 chemotherapy-treated patients and 7 trastuzumab plus chemotherapy–treated patients. However, no congestive heart failure events were reported. These data indicate that the addition of trastuzumab to chemotherapy significantly increased pCR rates in patients with operable HER2-positive breast cancer. (Buzdar AU, et al. J Clin Oncol. 2005;23:3676–3685)

 

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