Targeted Therapies

Timely Information for Practicing Hematologists and Oncologists

www.tgt-therapies.com

NOVEMBER 2005

CASTLEMAN DISEASE

Anti–interleukin (IL)-6 receptor antibody therapy. Castleman disease is a lymphoproliferative disorder characterized by lymphadenopathy, systemic constitutional symptoms, and severe wasting as the illness progresses. A dysregulated overproduction of IL-6 in patients with Castleman disease led Nishimoto and colleagues to investigate the effectiveness of therapy with a humanized anti–IL-6 receptor monoclonal antibody (MRA). Twenty-eight patients have been enrolled in this ongoing study and were treated with infusions of MRA 8 mg/kg given biweekly over 16 weeks. Therapy with MRA was found to alleviate lymphadenopathy, relieve constitutional symptoms, improve biochemical parameters, and increase body weight. Furthermore, 11 of 15 patients treated with oral corticosteroids were able to reduce their corticosteroid dose during MRA therapy. Adverse events were mild to moderate. These findings indicate that MRA therapy over 16 weeks improves the symptoms and biochemical abnormalities associated with Castleman disease. Further follow-up is ongoing. (Nishimoto N, et al. Blood. 2005;106:2627–2632.)

 

NON-SMALL CELL LUNG CANCER (NSCLC)

Epidermal growth factor receptor (EGFR) gene copy number and mutations and increased sensitivity to gefitinib. Bronchoalveolar carcinomas (BACs) and lung adenocarcinomas with bronchoalveolar features have previously been reported to be sensitive to EGFR tyrosine kinase inhibitors. Hirsch and others report an analysis of archival tumor tissue collected during a Southwest Oncology Group clinical trial of patients with advanced-stage BAC treated with gefitinib. Fluorescent in situ hybridization (FISH) was used to detect EGFR, and HER2 genes and gene copy number was correlated with clinical outcome (n = 81). Median overall survival was greater in EGFR/FISH-positive patients than EGFR/FISH-negative patients (not reached vs. 8 months; P = 0.042). EGFR copy number was also identified as a significant predictor for survival by multivariate analysis. No association between HER2 gene copy number and survival was found. In a second study, Takano and associates extracted DNA from surgical specimens of 66 patients with NSCLC who had experienced relapse after surgery. Pyrosequencing and quantitative real-time polymerase chain reaction were used to analyze the allelic pattern and EGFR and ErbB2 copy numbers. No ErbB2 mutations were identified; however 39 patients (59%) had EGFR mutations. Following subsequent therapy with gefitinib, patients with EGFR mutations had a higher response rate (P <0.0001), longer median time to progression (P <0.0001), and greater median survival time (P = 0.0001) than patients without EGFR mutations. In addition, increased EGFR copy number (≥3/cell) was found in 29 patients and was associated with a higher response rate (P = 0.005) and longer median time to progression (P = 0.038). These two studies demonstrated that increased EGFR copy number and EGFR mutations are associated with improved clinical outcomes in patients with NSCLC. (Hirsch FR, et al. J Clin Oncol. 2005;23:6838–6845; Takano T, et al. J Clin Oncol. 2005;23:6829–6837.)

 

MANTLE-CELL LYMPHOMA (MCL)

Rituximab plus alternating chemotherapy results in durable remissions. Hyper-CVAD (cyclophosphamide-vincristine-doxorubicin-dexamethasone) chemotherapy alternating with high-dose methotrexate and cytarabine has been shown to be effective in patients with aggressive MCL. Romaguera and coworkers treated patients who had newly diagnosed aggressive histopathologic variants of MCL with rituximab plus hyper-CVAD (cycles 1, 3, 5, and 7) chemotherapy alternating with rituximab plus high-dose methotrexate and cytarabine (cycles 2, 4, 6, and 8). Rituximab 375 mg/m2 was administered on the first day of each cycle. Among 97 evaluable patients, the response rate was 97%, and 87% of patients achieved a complete response (CR) or an unconfirmed CR. The 3-year failure-free survival rate for patients ≤65 years of age was 73% compared with 50% for patients aged >65 years (P = 0.02). The 3-year overall survival rate was 82% (median follow-up, 40 months). The principal toxicity was hematologic, and five patients died of acute toxicity. Four patients developed treatment-related myelodysplasia or acute myelogenous leukemias. These data suggest that rituximab plus alternating hyper-CVAD chemotherapy is an effective therapy for patients with previously untreated aggressive MCL. However, this regimen is not recommended as standard therapy for patients aged >65 years. Randomized phase III studies are needed to more clearly define the role of this regimen. (Romaguera JE, et al. J Clin Oncol. 2005;23:7013–7023.)

 

CHRONIC LYMPHOCYTIC LEUKEMIA (CLL)

Fludarabine plus alemtuzumab. Elter and others conducted a phase II study of 36 patients with relapsed or refractory B-cell CLL treated with fludarabine plus alemtuzumab (FluCam). The alemtuzumab dose was escalated on 3 consecutive days from 3 to 10 to 30 mg at the start of each cycle. FluCam (fludarabine 30 mg/m2 and alemtuzumab 30 mg) was given on the next 3 consecutive days. Treatment was administered every 28 days for up to six cycles. The response rate was 83% (11 CRs and 19 partial responses [PRs]). Two patients developed fungal pneumonias, two patients experienced subclinical reactivation of cytomegalovirus, and one patient died of Escherichia coli sepsis. This study demonstrated that FluCam therapy is effective in patients with relapsed or refractory B-cell CLL and has acceptable toxicity. (Elter T, et al. J Clin Oncol. 2005;23:7024–7031.)

 

HEPATOCELLULAR CARCINOMA (HCC)

Erlotinib therapy. Philip and associates treated 38 patients with unresectable or metastatic HCC (one prior systemic or locoregional therapy was allowed) with erlotinib, an EGFR/HER1 tyrosine kinase inhibitor. EGFR/HER1 expression was detected in the tumors of 88% of the patients. Disease control was observed in 59% of the patients, and three patients had a partial radiologic response. Median overall survival was 13 months. Grade 3 or 4 skin toxicity or diarrhea occurred in five and three patients, respectively. Additional studies of erlotinib in patients with advanced HCC are warranted. (Philip PA, et al. J Clin Oncol. 2005;23:6657–6663.)

 

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