BioOncology Watch

Timely Information for Practicing Physicians

 

december 2001

Anti-CD20 Monoclonal Antibody Therapy

Rituximab mechanism of action.  Beatriz Bellosillo and colleagues investigated the in vitro effect of rituximab, a chimeric monoclonal antibody directed against CD20, on cells from 55 patients with B-cell lymphoproliferative disorders.  A cytotoxic effect was not observed when cells were incubated with rituximab alone.  However, in the presence of human AB serum (as a source of complement), rituximab induced complement-dependent cell death (R-CDC).  Cytotoxic effects were observed in 4 of 4 patients with follicular lymphoma, 16 of 16 patients with mantle-cell lymphoma, 2 of 2 patients with hairy cell leukemia, and 9 of 33 patients with B-cell chronic lymphocytic leukemia.  The development of R-CDC was directly correlated with the number of CD20 molecules per cell and pre-incubation with anti-CD59 enhanced the cytotoxic effect of rituximab.  R-CDC was not found to activate caspase-3 or to cleave polyADP ribose polymerase.  In addition, R-CDC was associated with a rapid and intense production of reactive oxygen species (ROS) and was blocked by ROS scavengers.  These findings indicate that the cytotoxic effect of rituximab is mediated by a caspase-independent process involving the generation of superoxide radicals. Furthermore, CD20, CD59, and complement all have roles in the in vitro cytotoxicity of rituximab.  (Bellosillo B, et al. Blood 2001;98:2771-2777)

 

Pretargeted radioimmunotherapy (RIT).  Encouraging results have been seen with radiolabeled anti-CD20 monoclonal antibody treatments of patients with relapsed B-cell lymphomas.  However, normal tissue is exposed to radiation during the period required for the intravenously infused radioimmunoconjugate to circulate and accumulate at tumor sites.  Oliver Press and coworkers investigated the ability of a "pretargeting" approach to improve the biodistribution of radioactivity in mice bearing Ramos lymphoma xenografts.  This approach comprised an initial infusion of pretargeted streptavidin-conjugated anti-CD20 1F5 antibody followed 24 hours later by a biotinylated N-acetyl-galactosamine-containing clearing agent, followed 3 hours later by 111Indium-labeled DOTA-biotin. This pretargeting technique increased tumor/normal organ ratios of adsorbed radioactivity from £ 6:1 with the infusion of conventional 111Indium-1F5 to 56:1.  Further experiments demonstrated that, while ³ 400 uCi of conventional 90Yttrium-1F5 was associated with lethal toxicity in 100% of mice, up to 800 uCi of 90Yttrium-DOTA-biotin could be safely administered with the pretargeting approach resulting in an 89% cure rate for the mice.  These data suggest that the pretargeting strategy has the potential to improve anti-CD20 therapy and warrants further testing. (Press OW, et al. Blood 2001;98:2535-2543)

 

Acute Myelogenous Leukemia (AML)

Nuclear factor (NF)-kB expression.  Previous studies have shown that, while the transcriptional activator NF-kB is expressed in several malignant cell types, normal unstimulated human CD34+ hematopoietic progenitor cells do not express NF-kB.  Monica Guzman and associates isolated AML cells from patients and found NF-kB to be readily expressed by primary AML CD34+ cells.  Further detailed analyses showed NF-kB to be active in the AML stem cell population (CD34+/CD38-/CD123+).  Exposure of AML stem cells to the proteasome inhibitor MG-132, an inhibitor of NF-kB, induced rapid cell death (apoptosis), whereas normal hematopoietic stem cells were unaffected.  These preclinical data demonstrate that AML stem cells aberrantly express active NF-kB, which may provide an opportunity to devise leukemia-specific treatments. (Guzman ML, et al. Blood; 98:2301-2307)

 

Metastatic Melanoma

Phase I study of a chimeric monoclonal antibody (mAb).  The GD3 ganglioside antigen has been previously been found to be highly expressed on malignant melanoma cells.  Andrew Scott et al conducted a phase I dose-escalation study of KM871, a chimeric anti-GD3 mAb, in patients with metastatic melanoma.  Patients received 3 infusions of KM871 at 2-week intervals and 17 patients were entered into 5 dose levels (1, 5, 10, 20, and 40 mg/m2).  In the initial infusion, KM871 was trace-labeled with 111Indium for an assessment of biodistribution in vivo and biopsies of metastatic sites were performed on days 7 and 10.  No dose-limiting toxicity was observed at any dose level. Uptake of 111Indium-KM871 was detected in all melanoma lesions >1.5 cm while no normal tissue uptake was observed.  None of the patients developed human antichimeric antibody and the terminal plasma half-life of 111Indium-KM871 was 7.68 ± 2.94 days.  One patient experienced an objective clinical partial response of 11 months duration.  These findings indicate that this anti-GD3 mAb represents a potentially safe and effective therapy for patients with metastatic malignant melanoma.  (Scott AM, et al. J Clin Oncol 2001;19:3976-3987)

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