Targeted Therapies

Formerly BioOncology Watch

www.tgt-therapies.com

DECEMBER 2004

NON-HODGKIN'S LYMPHOMA (NHL)

Phase II study of denileukin diftitox.  Denileukin diftitox, a fusion protein combining diphtheria toxin and IL-2 that targets lymphoma and leukemia cells expressing the IL-2 receptor, has been shown to have activity in CD25+ cutaneous T-cell lymphoma.  Nam Dang et al evaluated the use of denileukin diftitox as therapy in 45 patients with relapsed or refractory B-cell NHL.  All patients had previously been treated with rituximab and 32 (71%) patients were refractory to the last chemotherapy treatment.  Three CRs and 8 PRs were achieved (overall response rate of 24.5%).  Objective response rates were similar in patients with CD25+ and CD25- histologies (22% and 29%, respectively).  For survivors with a median follow-up of 18 months (range, 9-28 months), the projected progression-free survival rate at 20 months was 24% (95% CI: 0%-60%).  Adverse events were low-grade and transient.  This study demonstrated that denileukin diftitox is active against both CD25+ and CD25- relapsed or refractory B-cell NHL.  Further evaluation of this agent in combination with other therapies is warranted.  (Dang NH, et al. J Clin Oncol 2004;22:4095-4102)

 

Rituximab plus fludarabine, cyclophosphamide, and mitoxantrone (FCM).  Roswitha Forstpointner and colleagues report their results from a multicenter, randomized study of the combination of an rituximab plus FCM chemotherapy (R-FCM) versus FCM alone for patients with relapsed or refractory follicular, mantle-cell, or lymphomaplasmocytoid lymphoma (N = 147).  Among 128 evaluable patients, a response rate of 79% (33% CRs and 45% PRs) was observed in R-FCM-treated patients compared to 58% (13% CRs and 45% PRs) in FCM-treated patients (p = 0.01).  Subgroup analyses revealed that R-FCM induced higher response rates than FCM alone in both the follicular and mantle-cell lymphoma populations.  Progression-free and overall survival times were also greater in the R-FCM treatment group (p =0.0381 and 0.0030, respectively).  Safety profiles were similar in both groups.  This study demonstrated that the addition of rituximab to combination FCM chemotherapy improved outcomes in this population of relapsed or refractory NHL patients.  Caution should be used in the interpretation of these data because FCM is a new combination instead of a standard therapy, the study population is a heterogeneous mixture of different NHL histologies, and there is a lack of information regarding therapies utilized subsequent to protocol treatment.  (Forstpointner R, et al. Blood 2004;104:3064-3071)

 

ACUTE MYELOID LEUKEMIA (AML)

Phase III study of all-trans retinoic acid (ATRA).  RF Schlenk and others from the AML Study Group ULM conducted a phase III study to evaluate the effect of combining ATRA with standard chemotherapy in elderly patients with AML.  AML patients aged ≥ 61 years (median, 66.6 years) were randomized to receive induction and consolidation chemotherapy with or without ATRA (N = 242).  Induction chemotherapy consisted of ICE (idarubicin, cytarabine, etoposide) ± ATRA and consolidation chemotherapy comprised HAM (cytarabine and mitoxantrone) ± ATRA.  Patients in CR were then randomized to a second intensive consolidation chemotherapy or to a 1-year oral maintenance chemotherapy.  Induction therapy with the ATRA-containing chemotherapy regimen was observed to have a greater CR rate compared to standard chemotherapy alone (52% vs. 39%; p = 0.05).  Event-free and overall survival times were also improved in ATRA-treated patients (p = 0.03 and 0.01, respectively).  Overall survival after the second randomization was greater in the intensive consolidation group compared to the maintenance group (p < 0.001).  These findings indicate that the addition of ATRA to standard induction and consolidation chemotherapy may improve treatment outcomes in elderly patients with AML.  (Schlenk RF, et al. Leukemia 2004;18:1798-1803)

 

MULTIPLE MYELOMA

Donor lymphocyte infusion (DLI) plus thalidomide.  Adoptive immunotherapy with DLI has become an accepted treatment option for multiple myeloma patients who relapse after allogeneic stem cell transplantation.  Response rates after DLI range from 30% to 50% and few CRs are achieved.  In the present phase 1/2 study, Nicolaus Kroger et al. added oral low-dose thalidomide (100 mg daily) to DLI therapy to determine if this combination would improve the antimyeloma effect of DLI in 18 myeloma patients who relapsed after allogeneic transplantation.  CR was achieved in 22% of patients and the overall response rate was 67%.  Thalidomide-related grade I/II weakness was seen in 68% of patients and grade I/II neuropathy occurred in 28% of patients.  No grade II-IV acute GvHD was observed and only 2 patients developed grade I acute GvHD.  Limited chronic GvHD was seen in 2 patients (11%).  These findings indicate that a strong anti-myeloma effect with a low incidence of GvHD can be induced by the combination of low-dose thalidomide and DLI.  (Kroger N, et al. Blood 2004;104:3361-3363)

 

WALDENSTRÖM’S  MACROGLOBULINEMIA (WM)

Paradoxical observations following rituximab treatments.  Rituximab is an important treatment for patients with WM.  Usual therapy consists of 4 weekly infusions of rituximab 375 mg/m2 and serum IgM levels are evaluated 12 weeks after treatment begins.  Steve Treon and colleagues describe an abrupt rise in serum IgM levels measured within 12 weeks of the start of rituximab therapy in 10 of 11 patients treated.  The mean serum IgM levels increased from 4,370 mg/dL at baseline to a peak of 5,865 mg/dL that occurred at a mean of 4 weeks after the initiation of treatment.  Mean serum viscosity levels also increased in 8 patients tested.  A subdural hemorrhage occurred in one patient whose rise in serum IgM level was associated with an increase in serum viscosity from 3.9 to 10.1 centipoise.  Two other patients experienced worsening headaches and epistaxis.  These data suggest that spikes in serum IgM levels commonly occur in WM patients shortly after initiation of rituximab treatment.  Careful monitoring is recommended and the mechanism of this effect is under investigation.  (Treon SP, et al. Ann Oncol 2004;15:1481-1483)

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